Steve Kymes

Company: Ionis Pharmaceuticals, Inc.
Job title: Director - Health Economics & Outcomes Research
Seminars:
Supporting Data-Driven Decisions with Real-World Evidence for Ultra- Rare Pediatric Neurological Diseases 10:30 am
Explore innovative approaches to generating real-world evidence in ultra-rare pediatric neurological conditions, where traditional data is limited Address challenges in evidence generation, including data availability, small sample sizes, data heterogeneity, and follow-up Drive regulatory, clinical, and access decision makers through cross-functional collaborations and data sources tailored to rare pediatric populationsRead more
day: Conference Day Two